First stem cell clinical trial for treating brain's "communication highway" to begin
UCSF researchers are set to begin a Phase I clinical trial in collaboration with StemCells, Inc. to test the safety and preliminary effectiveness of using neural stem cells to treat children with a rare, fatal form of a brain disorder known as Pelizaeus-Merzbacher disease (PMD). Currently, there are no effective treatments for the fatal forms of the disease, which affects males that inherit a single defective gene.